“We are committed to collaborating with the FDA to advance AMT-130 to patients and their families as rapidly as possible,” said Matt Kapusta, chief executive officer at uniQure. “The support we have …
FDA Minutes Confirm Challenging Path Ahead for UniQure’s Huntington’s ...
2 days ago · The final minutes from uniQure’s pre–biologics license application meeting with the FDA are in, and they confirm the company’s and analysts’ suspicions—it’s going to be a longer regulatory …
UniQure plummets, again, as FDA indicates it will reject Huntington's ...
But maybe there's supplemental data that could support the benefits of lowering HTT, the mutated gene responsible for Huntington's disease.
UniQure Shares Drop After More Negative News From FDA on Huntington's …
2 days ago · UniQure shares fell Thursday after the gene therapy company said its Huntington's disease drug hit more regulatory roadblocks. Shares of the Lexington, Mass., company fell 15% early …
uniQure N.V. Provides Regulatory Update on AMT-130 for Huntington's Disease
3 days ago · On December 4, 2025, uniQure N.V. announced a regulatory update on its gene therapy AMT-130 for Huntington's disease. Key Highlights: FDA feedback indicates Phase I/II data …
UniQure slides further on outlook for Huntington’s gene therapy
3 days ago · UniQure slides further on outlook for Huntington’s gene therapy Finalized minutes from a late-October meeting with the FDA confirm the agency doesn’t see the data collected so far as …
uniQure Provides Regulatory Update on AMT-130 for - GlobeNewswire
2 days ago · “The support we have seen these last weeks from the Huntington’s disease community, including patients, families, caregivers, clinicians and advocates reinforces the urgency of the unmet …
Huntington's disease support groups | Huntington's Disease News
Apr 25, 2025 · Finding a Huntington’s disease support group can help you connect with others who understand what you’re going through.
Huntington’s Disease: Everything You Need to Know
Support for Patients and Families Living with Huntington's Disease can be challenging, and support from healthcare professionals, genetic counselors, and support groups is crucial. Organizations such as …
Huntington’s Disease: Genetics, Symptoms, and ... - Los Angeles Times
Jun 17, 2025 · Learn about Huntington’s disease: its genetic causes, key symptoms, diagnosis, and what new research says about treatments and clinical trials.